What is AKU?

Alkaptonuria (AKU) is a genetic disease which damages the bones and cartilage, causes severe pain and leads to health problems such as osteoarthritis, heart disease and kidney infections. It is extremely rare and generally affects only one in every 250,000 people worldwide.

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What is DevelopAKUre?

DevelopAKUre is a clinical trial programme for the drug nitisinone, the first potential treatment for AKU. It is made up of 13 hospitals, pharmaceutical companies and consultancies, universities, biotech companies and national AKU patient groups.

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